Issue Date | Title | Author(s) | Relation | scopus | WOS | Fulltext/Archive link |
2006 | Enhanced efficacy of an AAV vector encoding chimeric, highly secreted acid alpha-glucosidase in glycogen storage disease type II | Sun, B.; Zhang, H.; Benjamin, D. K.; Brown, T.; Bird, A.; Young, S. P.; McVie-Wylie, A.; Chen, Y. T.; Koeberl, D. D. | Mol Ther 14(6), 822-830 | | | |
2011 | Enhanced efficacy of enzyme replacement therapy in Pompe disease through mannose-6-phosphate receptor expression in skeletal muscle | Koeberl, D. D.; Luo, X. Y.; Sun, B. D.; McVie-Wylie, A.; Dai, J.; Li, S. T.; Banugaria, S. G.; Chen, Y. T.; Bali, D. S. | Molecular Genetics and Metabolism 103, 107-112 | | | |
2001 | Recombinant human acid alpha-glucosidase enzyme therapy for infantile glycogen storage disease type II: results of a phase I/II clinical trial | Amalfitano, A.; Bengur, A. R.; Morse, R. P.; Majure, J. M.; Case, L. E.; Veerling, D. L.; Mackey, J.; Kishnani, P.; Smith, W.; McVie-Wylie, A.; Sullivan, J. A.; Hoganson, G. E.; Phillips, J. A.; Schaefer, G. B.; Charrow, J.; Ware, R. E.; Bossen, E. H.; Chen, Y. T. | Genet Med 3, 132-138 | | | |