公開日期 | 題名 | 作者 | 關聯 | scopus | WOS | 全文 |
2006 | Early, sustained efficacy of adeno-associated virus vector-mediated gene therapy in glycogen storage disease type Ia | Koeberl, D. D.; Sun, B. D.; Damodaran, T. V.; Brown, T.; Millington, D. S.; Benjamin, D. K.; Bird, A.; Schneider, A.; Hillman, S.; Jackson, M.; Beaty, R. M.; Chen, Y. T. | Gene Ther 13, 1281-1289 | | | |
2007 | Early, sustained efficacy of adeno-associated virus vector-mediated gene therapy in glycogen storage disease type Ia (vol 13, pg 1281, 2006) | Koeberl, D. D.; Sun, B. D.; Damodaran, T. V.; Brown, T.; Millington, D. S.; Benjamin, D. K.; Bird, A.; Schneider, A.; Hillman, S.; Jackson, M.; Beaty, R. M.; Chen, Y. T. | Gene Ther 14(3), 281 | | | |
2011 | Enhanced efficacy of enzyme replacement therapy in Pompe disease through mannose-6-phosphate receptor expression in skeletal muscle | Koeberl, D. D.; Luo, X. Y.; Sun, B. D.; McVie-Wylie, A.; Dai, J.; Li, S. T.; Banugaria, S. G.; Chen, Y. T.; Bali, D. S. | Molecular Genetics and Metabolism 103, 107-112 | | | |
2003 | Long-term correction of glycogen storage disease type II with a hybrid Ad-AAV vector | Sun, B. D.; Chen, Y. T.; Bird, A.; Amalfitano, A.; Koeberl, D. D. | Mol Ther 7, 193-201 | | | |
2003 | Packaging of an AAV vector encoding human acid alpha-glucosidase for gene therapy in glycogen storage disease type II with a modified hybrid adenovirus-AAV vector | Sun, B. D.; Chen, Y. T.; Bird, A.; Xu, F.; Hou, Y. X.; Amalfitano, A.; Koeberl, D. D. | Mol Ther 7, 467-477 | | | |