| Issue Date | Title | Author(s) | Relation | scopus | WOS | Fulltext/Archive link |
| 2002 | Efficacy of gene therapy for a prototypical lysosomal storage disease (GSD-II) is critically dependent on vector dose, transgene promoter, and the tissues targeted for vector transduction | Ding, E.; Hu, H.; Hodges, B. L.; Migone, F.; Serra, D.; Xu, F.; Chen, Y. T.; Amalfitano, A. | Mol Ther 5, 436-446 | | | |
| 2001 | Long-term efficacy after [E1-, polymerase-] adenovirus-mediated transfer of human acid-alpha-glucosidase gene into glycogen storage disease type II knockout mice | Ding, E. Y.; Hodges, B. L.; Hu, H.; McVie-Wylie, A. J.; Serra, D.; Migone, F. K.; Pressley, D.; Chen, Y. T.; Amalfitano, A. | Hum Gene Ther 12, 955-965 | | | |
| 2003 | Multiple muscles in the AMD quail can be ""cross-corrected"" of pathologic glycogen accumulation after intravenous injection of an [E1-, polymerase-] adenovirus vector encoding human acid-alpha-glucosidase | McVie-Wylie, A. J.; Ding, E. Y.; Lawson, T.; Serra, D.; Migone, F. K.; Pressley, D.; Mizutani, M.; Kikuchi, T.; Chen, Y. T.; Amalfitano, A. | J Gene Med 5, 399-406 | | | |
