公開日期 | 題名 | 作者 | 關聯 | scopus | WOS | 全文 |
---|---|---|---|---|---|---|
2003 | Packaging of an AAV vector encoding human acid alpha-glucosidase for gene therapy in glycogen storage disease type II with a modified hybrid adenovirus-AAV vector | Sun, B. D.; Chen, Y. T.; Bird, A.; Xu, F.; Hou, Y. X.; Amalfitano, A.; Koeberl, D. D. | Mol Ther 7, 467-477 | |||
2001 | Recombinant human acid alpha-glucosidase enzyme therapy for infantile glycogen storage disease type II: results of a phase I/II clinical trial | Amalfitano, A.; Bengur, A. R.; Morse, R. P.; Majure, J. M.; Case, L. E.; Veerling, D. L.; Mackey, J.; Kishnani, P.; Smith, W.; McVie-Wylie, A.; Sullivan, J. A.; Hoganson, G. E.; Phillips, J. A.; Schaefer, G. B.; Charrow, J.; Ware, R. E.; Bossen, E. H.; Chen, Y. T. | Genet Med 3, 132-138 | |||
1999 | Systemic correction of the muscle disorder glycogen storage disease type II after hepatic targeting of a modified adenovirus vector encoding human acid-alpha-glucosidase | Amalfitano, A.; McVie-Wylie, A. J.; Hu, H.; Dawson, T. L.; Raben, N.; Plotz, P.; Chen, Y. T. | Proc Natl Acad Sci U S A 96, 8861-8866 | |||
2000 | Towards a molecular therapy for glycogen storage disease type II (Pompe disease) | Chen, Y. T.; Amalfitano, A. | Mol Med Today 6, 245-251 |